Announcements

June 20th – World FSHD Day

Facioscapulohumeral Muscular Dystrophy – FSHD It is the third most common muscular dystrophy with a frequency of 1: 8,333 patients...

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Announcements

CHMP Recommends Translarna Label Update That Enables Treating DMD Patients Unable to Walk

June 30, 2020 The Committee for Medicinal Products for Human Use (CHMP), an arm of the European Medicines Agency, has recommended a label...

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Announcements, Uncategorized

Cure SMA – Virtual Annual Conference

The 2020 Annual SMA Conference is Going Virtual! JUNE 8 – 12, 2020 Use the link below to register for these free webinar events....

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